University of Florida Clinical Research Center

Gainesville, Florida 32611

3 studies enrolling now · 27 studies all time

What they study most

Charcot-Marie-Tooth Disease, Chronic Obstructive Pulmonary Disease, Chronic Pain, Combined Pulmonary Fibrosis and Emphysema, Cystic Fibrosis, Duchenne Muscular Dystrophy, Duchenne Muscular Dystrophy (DMD), Friedreich's Ataxia, Glycogen Storage Disease Type II, Glycogen Storage Disease Type II Infantile Onset, Interstitial Lung Disease, Late-onset Pompe Disease

Studies at this site

• A Phase 1/2 Study of VX-670 in Adult Participants With Myotonic Dystrophy 1 (DM1) — Recruiting now
• A Study to Evaluate the Safety, Efficacy, PK, PD and Immunogenicity of Cipaglucosidase Alfa/Miglustat in IOPD Subjects Aged 0 to <18 — Recruiting now
• MEK Inhibitor Mirdametinib (PD-0325901) in Patients With Neurofibromatosis Type 1 Associated Plexiform Neurofibromas — Running, not enrolling
• Efficacy and Safety of Seralutinib in Adult Subjects With PAH (PROSERA) — Completed
• Group Integrative Breathwork for Chronic Pain — Completed
• ADAPT - A Patient Registry of the Real-world Use of Orenitram® — Running, not enrolling
• A Study to Assess the Long-term Safety and Efficacy of ATB200/AT2221 in Adult Subjects With Late-Onset Pompe Disease (LOPD) — Completed
• A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec (SRP-9001) in a Previous Clinical Study — Enrolling by invitation
• ZIP Study-OL Study of Safety, PK, Efficacy, PD, Immunogenicity of ATB200/AT2221 in Pediatrics Aged 0 to < 18 y.o. w/LOPD — Running, not enrolling
• STRIDE Study - A Study in Subjects With LOPD Who Are Currently Being Treated With ERT — Stopped early
• Safety, Tolerability and Efficacy of ACTIMMUNE® Dose Escalation in Friedreich's Ataxia Study — Completed
• Safety, Tolerability and Efficacy of ACTIMMUNE® Dose Escalation in Friedreich's Ataxia — Completed
• Long-Term Safety Extension Study of ACTIMMUNE® (Interferon γ-1b) in Children and Young Adults With Friedreich's Ataxia — Completed
• Phase III Trial Assessing the Efficacy and Safety of PXT3003 in CMT1A Patients — Status unconfirmed
• A Phase 3 Adaptive Study to Evaluate the Safety and Efficacy of Inhaled Treprostinil in Participants With Pulmonary Hypertension (PH) Due to Chronic Obstructive Pulmonary Disease (COPD) — Stopped early
• An Open Label Extension Study to Evaluate Inhaled Treprostinil in Adult PH With ILD Including CPFE — Stopped early
• Safety and Efficacy of Inhaled Treprostinil in Adult PH With ILD Including CPFE — Completed
• Phase 3 Study to Evaluate the Efficacy & Safety of Self-Administered Injections of BMN165 by Adults With PKU — Completed
• Diet and Exercise in Pompe Disease — Completed
• A Study With BPS-314d-MR-PAH-303 in Participants With Pulmonary Arterial Hypertension — Stopped early
• Efficacy, Safety, and Tolerability Rollover Study of Eteplirsen in Subjects With Duchenne Muscular Dystrophy — Completed
• Assessment of Satiety Following Oral Administration of an Erythritol Sweetened Beverage — Completed
• An Open-Label Phase 3 Study of BMN 165 for Adults With PKU Not Previously Treated w/ BMN 165 — Completed
• A Pilot Study of Pyridostigmine in Pompe Disease — Stopped early
• Deflazacort Expanded Access Program for Children, Adolescents and Adults With Duchenne Muscular Dystrophy — APPROVED_FOR_MARKETING
• Vitamin B6 Effects for Women Taking Birth Control Pills — Completed
• Cough-Generated Aerosols of NTM in Cystic Fibrosis — Completed