A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec (SRP-9001) in a Previous Clinical Study

Enrolling by invitation · Phase 3

Conditions studied: Duchenne Muscular Dystrophy

In brief

The purpose of this study is to provide a single clinical study with a uniform approach to monitoring long-term safety and efficacy in participants who received delandistrogene moxeparvovec in a previous clinical study. No study drug will be administered as part of this study.

Key facts

Study ID

NCT05967351

Run by

Sarepta Therapeutics, Inc.

People needed

400

Starts

2023-09-27

Expected to finish

2033-10-31

Last updated by the study team

2026-02-06

Who can join

Age: any. Sex: male. Healthy volunteers: not accepted.

You may qualify if…

• Received delandistrogene moxeparvovec for Duchenne muscular dystrophy in a previous clinical study.
• Has (a) parent(s) or legal caregiver(s) or is ≥18 years of age and able to understand and comply with the study visit schedule and all other protocol requirements.

You may not qualify if…

• Not applicable

Where it is running

• Arkansas Children's Hospital — Little Rock, Arkansas, United States
• UCLA Medical Center — Los Angeles, California, United States
• Lucile Packard Children's Hospital Stanford (LPCH) — Palo Alto, California, United States
• University of California, Davis — Sacramento, California, United States
• Rady Children's Hospital — San Diego, California, United States
• Children's Hospital of Colorado — Aurora, Colorado, United States
• University of Florida Clinical Research Center — Gainesville, Florida, United States
• Ann & Robert H. Lurie Children's Hospital of Chicago — Chicago, Illinois, United States
• University of Iowa ICTS Clinical Research Unit — Iowa City, Iowa, United States
• The Johns Hopkins Hospital, Rubenstein Child Health Bldg — Baltimore, Maryland, United States
• Boston Children's Hospital — Boston, Massachusetts, United States
• Washington University School of Medicine — St Louis, Missouri, United States
• Columbia University Pediatric Neuromuscular Center — New York, New York, United States
• University of Rochester Medical Center — Rochester, New York, United States
• Lenox Baker Children's Hospital (Duke University) — Durham, North Carolina, United States
• Nationwide Children's Hospital — Columbus, Ohio, United States
• Oregon Health and Science University — Portland, Oregon, United States
• Chiildren's Hospital of Philadelphia — Philadelphia, Pennsylvania, United States
• Children's Health Specialty Center — Dallas, Texas, United States
• University of Utah Health — Salt Lake City, Utah, United States
• Children's Hospital of The King's Daughters — Norfolk, Virginia, United States
• Children's Hospital Wisconsin — Milwaukee, Wisconsin, United States
• Universitair Ziekenhuis Gent, Neuromuscular Reference Centre (NMRC) — Ghent, East Flanders, Belgium
• Universitätsklinikum Essen - Klinik für Kinderheilkunde I — Essen, North Rhine-Westphalia, Germany
• Hong Kong Children's Hospital — Hong Kong, Hong Kong

Full record on ClinicalTrials.gov

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