Deflazacort Expanded Access Program for Children, Adolescents and Adults With Duchenne Muscular Dystrophy
APPROVED_FOR_MARKETING
Conditions studied: Duchenne Muscular Dystrophy
In brief
The expanded access program will provide access to treatment with deflazacort in children, adolescent, and adult patients with DMD in the U.S. who are ineligible, unable, or otherwise unwilling to enroll in a clinical study examining the efficacy of deflazacort while a new drug application is under preparation and review. Enrollment is open to all eligible patients.
Key facts
- Study ID
- NCT02592941
- Run by
- PTC Therapeutics
- Last updated by the study team
- 2018-02-28
Who can join
Age: 5 and older. Sex: any. Healthy volunteers: not accepted.
Where it is running
- Phoenix Children's Hospital — Phoenix, Arizona, United States
- Arkansas Children's Hospital — Little Rock, Arkansas, United States
- UCLA Health — Los Angeles, California, United States
- Childrens Hospital of Orange County — Orange, California, United States
- UC Davis Medical Center — Sacramento, California, United States
- Children's Hospital Colorado — Aurora, Colorado, United States
- Children's National Medical Center — Washington D.C., District of Columbia, United States
- University of Florida Clinical Research Center — Gainesville, Florida, United States
- Nicklaus Children's Hospital — Miami, Florida, United States
- Shriner's Hospital for Children - Tampa — Tampa, Florida, United States
- Children's Healthcare of Atlanta- Scottish Rite — Atlanta, Georgia, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago — Chicago, Illinois, United States
- Rush University Medical Center — Chicago, Illinois, United States
- Shriner's Hospital for Children - Chicago — Chicago, Illinois, United States
- Carle Foundation Hospital — Urbana, Illinois, United States
- Riley Hospital for Children at IU Health — Indianapolis, Indiana, United States
- University of Iowa Hospitals and Clinics — Iowa City, Iowa, United States
- University of Kansas Medical Center — Kansas City, Kansas, United States
- Kennedy Krieger Institute — Baltimore, Maryland, United States
- Boston Children's Hospital — Boston, Massachusetts, United States
- University of Michigan Health System — Ann Arbor, Michigan, United States
- Wayne State University- Children's Hospital of Michigan — Detroit, Michigan, United States
- Helen DeVos Children's Hospital Neurology Clinic — Grand Rapids, Michigan, United States
- Gillette Children's Specialty Healthcare — Saint Paul, Minnesota, United States
- Las Vegas Clinic — Las Vegas, Nevada, United States
Full record on ClinicalTrials.gov
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