Clinical Trial Site

Jerusalem 92100

3 studies enrolling now · 10 studies all time

What they study most

ATTR Amyloidosis, Acid Cholesteryl Ester Hydrolase Deficiency, Type 2, Acid Lipase Deficiency, Cholesterol Ester Storage Disease, Genetic Disease, Kidney Diseases, LAL-Deficiency, LIPA Deficiency, Lysosomal Acid Lipase Deficiency, Primary Hyperoxaluria, Primary Hyperoxaluria Type 1, Primary Hyperoxaluria Type 1 (PH1)

Studies at this site

• TRITON-CM: A Study to Evaluate Nucresiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy — Recruiting now
• ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis) — Recruiting now
• Lysosomal Acid Lipase (LAL) Deficiency Registry — Recruiting now
• BONAPH1DE, A Prospective Observational Study of Patients With Primary Hyperoxaluria Type 1 (PH1) — Running, not enrolling
• A Study of Brepocitinib in Adults With Active, Non-Infectious, Non-Anterior Uveitis — Running, not enrolling
• HELIOS-B: A Study to Evaluate Vutrisiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy — Running, not enrolling
• A Study of Lumasiran in Infants and Young Children With Primary Hyperoxaluria Type 1 — Completed
• A Study to Evaluate Lumasiran in Children and Adults With Primary Hyperoxaluria Type 1 — Completed
• A Study to Evaluate DCR-PHXC in Children and Adults With Primary Hyperoxaluria Type 1 and Primary Hyperoxaluria Type 2 — Completed
• Trial of Andexanet in Patients Receiving an Oral FXa Inhibitor Who Require Urgent Surgery — Stopped early