Lysosomal Acid Lipase (LAL) Deficiency Registry
Recruiting now
Conditions studied: Lysosomal Acid Lipase Deficiency, Cholesterol Ester Storage Disease, Wolman Disease, Acid Cholesteryl Ester Hydrolase Deficiency, Type 2, Acid Lipase Deficiency, LIPA Deficiency, LAL-Deficiency
In brief
This is an observational, multi-center, international disease registry designed to collect longitudinal data and create a knowledge base that will be utilized to improve the care and treatment of patients with LAL Deficiency. Participation in the Registry by both physicians and patients is voluntary.
Key facts
- Study ID
- NCT01633489
- Run by
- Alexion Pharmaceuticals, Inc.
- People needed
- 300
- Starts
- 2013-05-30
- Expected to finish
- 2029-08-30
- Last updated by the study team
- 2026-03-06
Who can join
Age: any. Sex: any. Healthy volunteers: not accepted.
Where it is running
- Clinical Trial Site — Stanford, California, United States (enrolling)
- Clinical Trial Site — Miramar, Florida, United States (enrolling)
- Clinical Trial Site — Orlando, Florida, United States (enrolling)
- Clinical Trial Site — Atlanta, Georgia, United States (enrolling)
- Clinical Trial Site — Chicago, Illinois, United States (enrolling)
- Clinical Trial Site — Boston, Massachusetts, United States (enrolling)
- Clinical Trial Site — Detroit, Michigan, United States (enrolling)
- Clinical Trial Site — Minneapolis, Minnesota, United States (enrolling)
- Clinical Trial Site — Jackson, Mississippi, United States (enrolling)
- Clinical Trial Site — Hackensack, NJ, 7601, New Jersey, United States (enrolling)
- Clinical Trial Site — New York, New York, United States (enrolling)
- Clinical Trial Site — The Bronx, New York, United States (enrolling)
- Clinical Trial Site — Philadelphia, Pennsylvania, United States (enrolling)
- Clinical Trial Site — Philadelphia, Pennsylvania, United States (enrolling)
- Clinical Trial Site — Philadelphia, Pennsylvania, United States (enrolling)
- Clinical Trial Site — Houston, Texas, United States (enrolling)
- Clinical Trial Site — Houston, Texas, United States (enrolling)
- Clinical Trial Site — Snyder, Texas, United States (enrolling)
- Clinical Trial Site — Tacoma, Washington, United States (enrolling)
- Clinical Trial Site — New Lambton Heights, New South Wales, Australia (enrolling)
- Clinical Trial Site — Ghent, East Flanders, Belgium (enrolling)
- Clinical Trial Site — Campinas, São Paulo, Brazil (enrolling)
- Clinical Trial Site — São Paulo, Brazil (enrolling)
- Clinical Trial Site — São Paulo, Brazil (enrolling)
- Clinical Trial Site — Phoenix, Arizona, United States (enrolling)
Full record on ClinicalTrials.gov
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