National Neuromuscular Research Institute

Austin, Texas 78759-8402

6 studies enrolling now · 15 studies all time

What they study most

AChR-Ab Seropositive Generalized Myasthenia Gravis, Amyloid Cardiomyopathy, Amyloidosis, Amyotrophic Lateral Sclerosis, Becker Muscular Dystrophy, CIDP, Cardiomyopathies, Charcot-Marie-Tooth Disease, Chronic Inflammatory Demyelinating Polyneuropathy, Chronic Inflammatory Demyelinating Polyradiculoneuropathy, Generalized Myasthenia Gravis, Generalized Myasthenia Gravis (gMG)

Studies at this site

• Acoramidis Transthyretin Amyloidosis Prevention Trial in the Young (ACT-EARLY) Study in Asymptomatic Carriers of a Pathogenic TTR Variant — Recruiting now
• ADAPT Forward - Master Protocol of a Platform Study to Evaluate the Safety and Efficacy of Multiple Regimens in Participants With Myasthenia Gravis — Recruiting now
• ADAPT Forward 1 - ISA1 - a Study to Evaluate Empasiprubart IV as add-on Therapy to Efgartigimod IV in Participants With AChR-Ab Seropositive Generalized Myasthenia Gravis With a Partial Clinical Response to Efgartigimod — Recruiting now
• A Study to Assess the Efficacy and Safety of Empasiprubart in Adults With CIDP — Recruiting now
• A Non-interventional, Post-authorisation Safety Study of Patients Treated With Efgartigimod Alfa — Recruiting now
• Open-Label Extension of EDG-5506 in Participants With Becker Muscular Dystrophy — Enrolling by invitation
• Phase 2 Study of EDG-5506 in Becker Muscular Dystrophy (GRAND CANYON) — Running, not enrolling
• A Study to Test How Safe Pozelimab and Cemdisiran Combination Therapy and Cemdisiran Alone Are and How Well They Work in Adult Patients With Generalized Myasthenia Gravis — Running, not enrolling
• A Study to Assess Efficacy and Safety of Efgartigimod PH20 SC in Adults With Ocular Myasthenia Gravis — Running, not enrolling
• A Study to Assess the Efficacy and Safety of Empasiprubart Versus IVIg in Adults With Multifocal Motor Neuropathy — Running, not enrolling
• A Study to Assess Adults With CIDP Transitioning From IVIg to Efgartigimod PH20 SC — Completed
• A Study of STRO4 in Patients Amyotrophic Lateral Sclerosis (ALS) — Stopped early
• A Phase 3 Study to Evaluate the Efficacy and Safety of Efgartigimod IV in Patients With Acetylcholine Receptor Binding Antibody Seronegative Generalized Myasthenia Gravis — Running, not enrolling
• Study to Assess the Effects of PTC857 Treatment in Participants With Amyotrophic Lateral Sclerosis ALS — Stopped early
• Phase III Trial Assessing the Efficacy and Safety of PXT3003 in CMT1A Patients — Status unconfirmed