Phase 2 Study of EDG-5506 in Becker Muscular Dystrophy (GRAND CANYON)
Running, not enrolling · Phase 2 · Has a placebo group
Conditions studied: Becker Muscular Dystrophy
In brief
A study of sevasemten (EDG-5506) in Becker muscular dystrophy (known as CANYON) and pivotal cohort (known as GRAND CANYON). The EDG-5506-201 CANYON study was expanded to include an additional 120 adult participants in a cohort called GRAND CANYON, that is a multicenter, randomized, double-blind, placebo-controlled study to evaluate the safety and efficacy of sevasemten in adults with Becker. CANYON and GRAND CANYON are fully enrolled.
Key facts
- Study ID
- NCT05291091
- Run by
- Edgewise Therapeutics, Inc.
- People needed
- 244
- Starts
- 2022-11-10
- Expected to finish
- 2026-09-01
- Last updated by the study team
- 2026-07-31
Who can join
Age: 12 and older, up to 50. Sex: male. Healthy volunteers: not accepted.
Where it is running
- UC San Diego — La Jolla, California, United States
- UCLA Medical Center — Los Angeles, California, United States
- UC Irvine Medical Center — Orange, California, United States
- Stanford Neuroscience Health Center — Palo Alto, California, United States
- UC Davis Medical Center — Sacramento, California, United States
- UC Denver — Aurora, Colorado, United States
- University of Florida — Gainesville, Florida, United States
- Rare Disease Research — Atlanta, Georgia, United States
- Northwestern University — Chicago, Illinois, United States
- Indiana University School of Medicine — Indianapolis, Indiana, United States
- University of Iowa — Iowa City, Iowa, United States
- University of Kansas Medical Center — Kansas City, Kansas, United States
- Kennedy Krieger Institute — Baltimore, Maryland, United States
- University of Massachusetts Memorial Medical Center — Worcester, Massachusetts, United States
- University of Minnesota — Minneapolis, Minnesota, United States
- Washington University School of Medicine — St Louis, Missouri, United States
- University of Rochester Medical Center — Rochester, New York, United States
- Rare Disease Research, LLC NC — Hillsborough, North Carolina, United States
- University of Cincinnati Gardner Neuroscience Institute — Cincinnati, Ohio, United States
- Nationwide Children's Hospital — Columbus, Ohio, United States
- University of Pennsylvania — Philadelphia, Pennsylvania, United States
- University of Pittsburgh — Pittsburgh, Pennsylvania, United States
- National Neuromuscular Research Institute — Austin, Texas, United States
- Neurology Rare Disease Center — Denton, Texas, United States
- Arkansas Children's Hospital — Little Rock, Arkansas, United States
Full record on ClinicalTrials.gov
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