Clinical Trial Site

Stanford, California 94305

3 studies enrolling now · 5 studies all time

What they study most

Acid Cholesteryl Ester Hydrolase Deficiency, Type 2, Acid Lipase Deficiency, Amyloid Neuropathies, Amyloid Neuropathies, Familial, Amyloidosis, Hereditary, Amyloidosis, Hereditary, Transthyretin-Related, Cholesterol Ester Storage Disease, Familial Transthyretin Cardiac Amyloidosis, LAL-Deficiency, LIPA Deficiency, Lysosomal Acid Lipase Deficiency, Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC)

Studies at this site

• TRITON-CM: A Study to Evaluate Nucresiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy — Recruiting now
• Lysosomal Acid Lipase (LAL) Deficiency Registry — Recruiting now
• A Study to Evaluate Vutrisiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy — Enrolling by invitation
• HELIOS-B: A Study to Evaluate Vutrisiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy — Running, not enrolling
• ENDEAVOUR: Phase 3 Multicenter Study of Revusiran (ALN-TTRSC) in Patients With Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC) — Completed