British Columbia Children's Hospital

Vancouver V6H 3V4

4 studies enrolling now · 22 studies all time

What they study most

Acute Myeloid Leukemia, Adolescent Idiopathic Scoliosis, Angelman Syndrome, Beta-Thalassemia, Cerebral Palsy, Chronic Pain, Cystic Fibrosis, Dravet Syndrome, Generalized Myasthenia Gravis, Genetic Diseases, Inborn, Hematologic Diseases, Hemoglobinopathies

Studies at this site

• REVEAL: A Phase 3 Study of ION582 in Angelman Syndrome — Recruiting now
• Evaluating the Pharmacokinetics, Pharmacodynamics, and Safety of Efgartigimod Administered Intravenously in Children With Generalized Myasthenia Gravis — Recruiting now
• A Longitudinal Study Looking at the Prevalence, Risk Factors & Consequences of Persistent Post-surgical Pain in Children — Recruiting now
• Phase 3 Efficacy and Safety Study of GTX-102 in Pediatric Subjects With Angelman Syndrome (AS) — Running, not enrolling
• A Study Evaluating the Long-term Safety and Efficacy of VX-121 Combination Therapy — Running, not enrolling
• Evaluation of VX-121/Tezacaftor/Deutivacaftor in Cystic Fibrosis (CF) Participants 1 Through 11 Years of Age — Running, not enrolling
• Evaluation of Long-Term Safety and Efficacy of Vanzacaftor/Tezacaftor/Deutivacaftor in Cystic Fibrosis Participants 1 Year of Age and Older — Enrolling by invitation
• Safety and Efficacy of Quizartinib in Children and Young Adults With Acute Myeloid Leukemia (AML), a Cancer of the Blood — Running, not enrolling
• Evaluation of Long-term Safety and Efficacy of ELX/TEZ/IVA in Cystic Fibrosis (CF) Participants 2 Years and Older — Completed
• Natural History Study of Exocrine Pancreatic Function in Infants With Cystic Fibrosis (CF) — Completed
• A Safety and Efficacy Study Evaluating CTX001 in Participants With Transfusion-Dependent β-Thalassemia — Completed
• This Study Will Investigate the Efficacy and Safety of A4250 in Children With PFIC Types 1 or 2 — Completed
• An Open-Label Extension Trial to Assess the Long-Term Safety of ZX008 (Fenfluramine Hydrochloride HCl) Oral Solution in Children and Young Adults With Dravet Syndrome — Completed
• A Study of VX-121 Combination Therapy in Participants With Cystic Fibrosis (CF) Who Are Homozygous for F508del, Heterozygous for F508del and a Gating (F/G) or Residual Function (F/RF) Mutation, or Have At Least 1 Other Triple Combination Responsive (TCR) CFTR Mutation and No F508del Mutation — Completed
• Adolescent Idiopathic Scoliosis Outcomes Database Registry — Status unconfirmed
• Prospective Database Registry Study of Scoliosis in Children With Cerebral Palsy — Status unconfirmed
• A Trial of Temsirolimus With Etoposide and Cyclophosphamide in Children With Relapsed Acute Lymphoblastic Leukemia and Non-Hodgkins Lymphoma — Completed
• Evaluation of ELX/TEZ/IVA in Cystic Fibrosis (CF) Subjects 2 Through 5 Years — Completed
• TruGraf and TRAC In Pediatrics Study — Status unconfirmed
• Trial of Nelarabine, Etoposide and Cyclophosphamide in Relapsed T-cell ALL and T-cell LL — Stopped early
• Study of Ataluren in Nonsense Mutation Cystic Fibrosis (ACT CF) — Completed
• Extension Study of Ataluren in Participants With Nonsense Mutation Cystic Fibrosis — Stopped early