Evaluation of Long-Term Safety and Efficacy of Vanzacaftor/Tezacaftor/Deutivacaftor in Cystic Fibrosis Participants 1 Year of Age and Older
Enrolling by invitation · Phase 3
Conditions studied: Cystic Fibrosis
In brief
The purpose of this study is to evaluate the long-term safety, tolerability, and efficacy of vanzacaftor/tezacaftor/deutivacaftor (VNZ/TEZ/D-IVA) in participants with cystic fibrosis (CF).
Key facts
- Study ID
- NCT05844449
- Run by
- Vertex Pharmaceuticals Incorporated
- People needed
- 174
- Starts
- 2023-08-11
- Expected to finish
- 2029-07-30
- Last updated by the study team
- 2026-04-29
Who can join
Age: 1 and older. Sex: any. Healthy volunteers: not accepted.
Where it is running
- Children's Hospital of Orange County — Orange, California, United States
- Stanford University - Palo Alto - Pulmonology — Palo Alto, California, United States
- Children's Hospital of Colorado - Pulmonology — Aurora, Colorado, United States
- The Emory Clinic - Clifton Road - Pulmonology — Atlanta, Georgia, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago - Hematology — Chicago, Illinois, United States
- JW Riley Hospital for Children - Pulmonology — Indianapolis, Indiana, United States
- Boston Children's Hospital — Boston, Massachusetts, United States
- Children's Health Care d/b/a Children's Hospitals and Clinics of Minnesota — Minneapolis, Minnesota, United States
- The Children's Mercy Hospital — Kansas City, Missouri, United States
- St. Louis Children's Hospital - Pulmonology — St Louis, Missouri, United States
- Cohen Children's Medical Center - Lakeville Road — Lake Success, New York, United States
- Cincinnati Children's Hospital Medical Center - Pulmonology — Cincinnati, Ohio, United States
- UH Cleveland Medical Center - Pulmonology — Cleveland, Ohio, United States
- Nationwide Children's Hospital — Columbus, Ohio, United States
- Children's Hospital of Pittsburgh - Pulmonology — Pittsburgh, Pennsylvania, United States
- Texas Children's Hospital - Wallace Tower - Pulmonology — Houston, Texas, United States
- Vermont Lung Center — Colchester, Vermont, United States
- American Family Childrens Hospital — Madison, Wisconsin, United States
- The Kids Research Institute Australia — Nedlands, Australia
- Women's & Children's Hospital — North Adelaide, Australia
- The Royal Children's Hospital Melbourne — Parkville, Australia
- Children's Health Queensland Hospital and Health Service — South Brisbane, Australia
- Hospital for Sick Children - Pulmonology — Toronto, Canada
- British Columbia Children's Hospital — Vancouver, Canada
- Hopital Femme Mere-Enfant — Bron, France
Full record on ClinicalTrials.gov
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