A Study Evaluating the Long-term Safety and Efficacy of VX-121 Combination Therapy
Running, not enrolling · Phase 3
Conditions studied: Cystic Fibrosis
In brief
The purpose of this study is to evaluate the long-term safety, tolerability, and efficacy of VX-121/tezacaftor/deutivacaftor (VX-121/TEZ/D-IVA) in participants with cystic fibrosis.
Key facts
- Study ID
- NCT05444257
- Run by
- Vertex Pharmaceuticals Incorporated
- People needed
- 822
- Starts
- 2022-11-08
- Expected to finish
- 2026-10-30
- Last updated by the study team
- 2026-07-21
Who can join
Age: 12 and older. Sex: any. Healthy volunteers: not accepted.
Where it is running
- Banner University of Arizona Medical Center — Tucson, Arizona, United States
- University of Arkansas for Medical Sciences — Little Rock, Arkansas, United States
- Miller Children's Hospital / Long Beach Memorial — Long Beach, California, United States
- Children's Hospital Los Angeles — Los Angeles, California, United States
- Kaiser Permanente — Oakland, California, United States
- University of California Davis Medical Center — Sacramento, California, United States
- University of California San Francisco, Lung Transplant Program — San Francisco, California, United States
- Children's Hospital of Colorado — Aurora, Colorado, United States
- National Jewish Health — Denver, Colorado, United States
- University of Florida, Shands Hospital — Gainesville, Florida, United States
- Joe DiMaggio Cystic Fibrosis & Pulmonary Center — Hollywood, Florida, United States
- University of Miami Miller School of Medicine — Miami, Florida, United States
- Central Florida Pulmonary Group,PA — Orlando, Florida, United States
- Nemours Children's Specialty Care — Pensacola, Florida, United States
- Johns Hopkins All Children's Hospital Outpatient Care Center — St. Petersburg, Florida, United States
- The Emory Clinic at Chantilly — Atlanta, Georgia, United States
- Augusta University — Augusta, Georgia, United States
- St. Luke's Cystic Fibrosis Center of Idaho — Boise, Idaho, United States
- Northwestern Memorial Hospital — Chicago, Illinois, United States
- Indiana University — Indianapolis, Indiana, United States
- Riley Hospital for Children at Indiana University Health — Indianapolis, Indiana, United States
- University of Kansas Medical Center — Kansas City, Kansas, United States
- University of Kentucky — Lexington, Kentucky, United States
- Tulane Medical Center — New Orleans, Louisiana, United States
- University of Alabama at Birmingham — Birmingham, Alabama, United States
Full record on ClinicalTrials.gov
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