The children's hospital of Philadelphia

Philadelphia, Pennsylvania 19403

48 studies enrolling now · 380 studies all time

What they study most

4H Syndrome, ACL Repair, ADA SCID, ADA-SCID, ADLD, AGS, ALD, ALD (Adrenoleukodystrophy), ALD Gene Mutation, ALSP, AMN, ARGI Deficiency

Studies at this site

• Study of the ITK Inhibitor Soquelitinib to Reduce Lymphoproliferation and Improve Cytopenias in Autoimmune Lymphoproliferative Syndrome (ALPS)-FAS Patients — Recruiting now
• A First-in-human Study of S230815 in Pediatric Participants With KCNT1-related Developmental and Epileptic Encephalopathy — Recruiting now
• A Study of Mavorixafor in Participants With Congenital and Acquired Primary Autoimmune and Idiopathic Chronic Neutropenic Disorders Who Are Experiencing Recurrent and/or Serious Infections — Recruiting now
• Patiromer for Treatment of Hyperkalaemia in Children Under 12 Years of Age — Recruiting now
• Phase 2b Study of RPT904 as Monotherapy in Participants With IgE-Mediated Food Allergy — Recruiting now
• Primary Sclerosing Cholangitis in Children — Recruiting now
• SAFety and Efficacy of Human Anti-thymocyte ImmunoGlobUlin SAB-142 ARresting Progression of Type 1 Diabetes — Recruiting now
• A Study of EPX-100 (Clemizole Hydrochloride) in Participants With Dravet Syndrome — Recruiting now
• Efficacy of KL1333 in Adult Patients With Primary Mitochondrial Disease — Recruiting now
• A U.S. Registry of Eosinophilic Esophagitis Pediatric, Adolescent and Adult Patients Treated With DUPIXENT® As Standard of Care — Recruiting now
• Collaboration for Down Syndrome Progress (CDP) — Recruiting now
• BELUGA: Better to Exchange ETT for LMA Before Extubation in Children Under General Anaesthesia — Recruiting now
• A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy — Recruiting now
• Evaluation of 18F-Fluciclovine Positron Emission Tomography - Magnetic Resonance Imaging (PET-MRI) in LGG — Recruiting now
• Pharmacokinetics, Efficacy, and Safety of Encaleret in Pediatric Participants With Autosomal Dominant Hypocalcemia Type 1 (ADH1) — Recruiting now
• Home Apnea Testing in CHildren Trial — Recruiting now
• Chronic Kidney Disease in Children Prospective Cohort Study (CKiD) — Recruiting now
• Intraoperative Contrast-Enhanced Ultrasound Evaluation of Blood Flow at the Time of Surgical Hip Reduction for DDH — Recruiting now
• Pediatric Acute Respiratory Distress Syndrome (ARDS) Management Trial — Recruiting now
• Validation of Oxygen Nanosensor in Mitochondrial Myopathy — Recruiting now
• Validation of Nanosensor Oxygen Measurement — Recruiting now
• Studying the Presence of CFRD Complications With Thoughtful Recruitment (SPeCTRuM) — Recruiting now
• Neurometabolic Profile of Individuals With Primary Mitochondrial Disease — Recruiting now
• North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC) — Recruiting now
• Improving Safety and Quality of Tracheal Intubation Practice in Pediatric ICUs — Recruiting now
• STXBP1 and SYNGAP1 Related Disorders Natural History Study — Recruiting now
• The Myelin Disorders Biorepository Project — Recruiting now
• Efficacy and Safety of Phentermine/Topiramate in Youth With Hypothalamic Obesity — Recruiting now
• Esophageal String Test Monitoring to Monitor Eosinophilic Esophagitis During Oral Immunotherapy — Recruiting now
• The Pediatric Anesthesia Quality Improvement Project — Recruiting now
• SHAPE of Portal Hypertension in Children — Recruiting now
• Non-Invasive Diagnosis of Pediatric Pulmonary Invasive Mold Infections — Recruiting now
• The ENERGY Study: Evaluation of Safety and Tolerability of INZ-701 in Infants With ENPP1 Deficiency or ABCC6 Deficiency — Running, not enrolling
• The PediQUEST Response Intervention Study — Completed
• Biologic Abatement and Capturing Kids' Outcomes and Flare Frequency in Juvenile Spondyloarthritis — Completed
• Extension Trial Evaluating the Long-term Safety and Efficacy of Dasiglucagon in Children With Congenital Hyperinsulinism — Completed
• The REPLACE Registry for Cholbam® (Cholic Acid) — Running, not enrolling
• Tacrolimus/Everolimus vs. Tacrolimus/MMF in Pediatric Heart Transplant Recipients Using the MATE Score — Completed
• Efficacy and Safety of Encaleret Compared to Standard of Care in Participants With ADH1 — Running, not enrolling
• TReatment for ImmUne Mediated PathopHysiology — Running, not enrolling
• The AYA Oncology Self-care Movement — Starting soon
• Observational Approach Versus Surgical Intervention for Stones — Starting soon
• Study to Evaluate the Safety and Efficacy of PF-06939926 for the Treatment of Duchenne Muscular Dystrophy — Running, not enrolling
• Reduced Intensity Conditioning (RIC) Regimen for Patients With Non-malignant Disorders — Completed
• A Study to Evaluate Safety and Efficacy of Ocrelizumab in Comparison With Fingolimod in Children and Adolescents With Relapsing-remitting Multiple Sclerosis (RRMS) — Running, not enrolling
• A Registry for Participants With Chronic Hypoparathyroidism — Completed
• Genetic Collection Protocol — Completed
• Open-Label Study of 18F-mFBG for Imaging Neuroblastoma — Running, not enrolling
• Efficacy and Safety of Odevixibat in Children With Biliary Atresia Who Have Undergone a Kasai HPE (BOLD) — Completed
• Open-Label Extension Study of BBP-418 (Ribitol) for LGMD2I/R9 — Running, not enrolling