A Study of Mavorixafor in Participants With Congenital and Acquired Primary Autoimmune and Idiopathic Chronic Neutropenic Disorders Who Are Experiencing Recurrent and/or Serious Infections
Recruiting now · Phase 3 · Has a placebo group
Conditions studied: Neutropenia
In brief
The purpose of this study is to demonstrate the efficacy and evaluate the safety and tolerability of mavorixafor in participants with congenital or acquired primary autoimmune and idiopathic chronic neutropenic disorders who are experiencing recurrent and/or serious infections as assessed by demonstrating its clinical benefit and increasing levels of circulating neutrophils.
Key facts
- Study ID
- NCT06056297
- Run by
- X4 Pharmaceuticals
- People needed
- 176
- Starts
- 2024-06-06
- Expected to finish
- 2027-11-01
- Last updated by the study team
- 2026-08-06
Who can join
Age: 12 and older. Sex: any. Healthy volunteers: not accepted.
Where it is running
- Phoenix Children's Hospital — Phoenix, Arizona, United States (enrolling)
- Orso Health — La Jolla, California, United States (enrolling)
- University of California, Los Angeles-UCLA — Los Angeles, California, United States (enrolling)
- UC Irvine — Irvine, California, United States (enrolling)
- University of Southern Florida — St. Petersburg, Florida, United States (enrolling)
- Children's Healthcare of Atlanta (CHOA) — Atlanta, Georgia, United States (enrolling)
- University of Iowa — Iowa City, Iowa, United States (enrolling)
- Boston Children's Cancer Center — Boston, Massachusetts, United States (enrolling)
- University of Michigan — Ann Arbor, Michigan, United States (enrolling)
- Washington University — St Louis, Missouri, United States (enrolling)
- Duke University Medical Center — Durham, North Carolina, United States (enrolling)
- Cincinnati Children's Hospital Medical Center — Cincinnati, Ohio, United States (enrolling)
- Cleveland Clinic — Cleveland, Ohio, United States (enrolling)
- The Children's Hospital of Philadelphia — Philadelphia, Pennsylvania, United States (enrolling)
- St. Jude Childrens; Research Hospital — Memphis, Tennessee, United States (enrolling)
- UT Southwestern Medical Center — Dallas, Texas, United States (enrolling)
- Cook Children's Medical Center — Fort Worth, Texas, United States (enrolling)
- Texas Children's Hospital/ Baylor College of Medicine — Houston, Texas, United States (enrolling)
- Sarah Cannon Research Institute — Woodland, Texas, United States (enrolling)
- University of Utah — Salt Lake City, Utah, United States (enrolling)
- Froedtert And Medical College Of Wisconsin — Milwaukee, Wisconsin, United States (enrolling)
- Hospital El Cruce — Buenos Aires, Argentina (enrolling)
- Instituto de Investigaciones Clínicas Córdoba — Córdoba, Argentina (enrolling)
- Santorio 9 de Julio — San Miguel de Tucumán, Argentina (enrolling)
- Perth Children's Hospital — Nedlands, Australia (enrolling)
Full record on ClinicalTrials.gov
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