Ospedale Pediatrico Bambino Gesù

Roma 165

10 studies enrolling now · 31 studies all time

What they study most

AOSD, Acute-graft-versus-host Disease, Adenovirus Infection, Alexander Disease, Alport Syndrome, Angelman Syndrome, Antibiotic Stewardship, Arginase I Deficiency, BK Virus Infection, Biliary Atresia, Bronchiectasis, Chronic Kidney Disease

Studies at this site

A Study to Find Out How EMPAgliflozin is Tolerated and if it Helps Children and Adolescents With Chronic KIDNEY Disease (EMPA-KIDNEY® Kids) — Recruiting now
The AIRTIVITY™ Study: A Study to Find Out Whether BI 1291583 Helps People With Bronchiectasis — Recruiting now
A Double-blind Study Evaluating the Efficacy, Safety, and Tolerability of Zorevunersen in Patients With Dravet Syndrome — Recruiting now
A Study to Find Out How Nerandomilast is Tolerated, Handled by the Body, and if it Helps Children and Adolescents With Interstitial Lung Disease (FIBRONEER-chILD) — Recruiting now
REVEAL: A Phase 3 Study of ION582 in Angelman Syndrome — Recruiting now
A Platform Trial for Pediatric Participants With Obesity or Overweight (LY900040) — Recruiting now
A Research Study Looking at Long-term Treatment With Mim8 in People With Haemophilia A — Recruiting now
Study of Sparsentan Treatment in Pediatrics With Proteinuric Glomerular Diseases — Recruiting now
Lung Ultrasound for Guiding Antibiotic Use in Pediatric Pneumonia — Recruiting now
Global Patient Registry to Monitor Long-term Safety and Effectiveness of Increlex® in Children and Adolescents With Severe Primary Insulin-like Growth Factor-1 Deficiency (SPIGFD). — Recruiting now
Efficacy and Safety of Odevixibat in Children With Biliary Atresia Who Have Undergone a Kasai HPE (BOLD) — Completed
A 12-Month Study of Lasmiditan (LY573144) Treatment in Children Aged 6 to 17 With Migraine — Stopped early
Phase 3 Efficacy and Safety Study of BG00012 in Pediatric Participants With Relapsing-Remitting Multiple Sclerosis (RRMS) — Completed
A Study of Recombinant Von Willebrand Factor (rVWF) With or Without ADVATE in Children With Severe Von Willebrand Disease (VWD) — Completed
A Study of Etavopivat in Adults and Adolescents With Sickle Cell Disease (HIBISCUS) — Running, not enrolling
A Study to Evaluate the Safety and Efficacy of Zilganersen (ION373) in Patients With Alexander Disease (AxD) — Running, not enrolling
A Study of Lasmiditan (LY573144) Treatment in Children Aged 6 to 17 With Migraine — Stopped early
Evaluate Efficacy, Safety and Tolerability, PK and PD of Emapalumab in Children and Adults With MAS in Still's or SLE — Completed
A Study of Galcanezumab (LY2951742) in Participants 6 to 17 Years of Age With Episodic Migraine — Running, not enrolling
A Safety Study for Previously Treated Vatiquinone (PTC743) Participants With Inherited Mitochondrial Disease — Completed
A Study of Recombinant Von Willebrand Factor (rVWF) in Pediatric and Adult Participants With Severe Von Willebrand Disease (VWD) — Completed
Efficacy and Safety of Pegzilarginase in Patients With Arginase 1 Deficiency — Completed
Study to Evaluate Viralym-M (ALVR105) for the Treatment of Virus-Associated Hemorrhagic Cystitis (HC) — Stopped early
Posoleucel (ALVR105) for the Treatment of Adenovirus Infection in Pediatric and Adult Participants Receiving Standard of Care Following Allogeneic Hematopoietic Cell Transplantation — Stopped early
Rofecoxib Efficacy and Safety Evaluation Trial in Hemophilic Arthropathy — Stopped early
Study Comparing Efficacy and Safety of Defibrotide vs Best Supportive Care in the Prevention of Hepatic Veno-Occlusive Disease in Adult and Pediatric Patients — Completed
An Open-Label Study of Defibrotide for the Prevention of Acute Graft-versus-Host-Disease (AGvHD) — Completed
rVWF IN PROPHYLAXIS — Completed
Short Term Observational Study in DEB Patients — Completed
Effects of Livoletide (AZP-531) on Food-related Behaviors in Patients With Prader-Willi Syndrome — Stopped early
Open-Label Study of Asfotase Alfa in Infants and Children ≤ 5 Years of Age With Hypophosphatasia (HPP) — Completed