Ionis Investigative Site

Amsterdam 1105AZ

2 studies enrolling now · 6 studies all time

What they study most

Familial Chylomicronemia Syndrome, Hereditary Angioedema, Pelizaeus-Merzbacher Disease

Studies at this site

• Rocket Study: A Study to Characterize Biomarkers and Disease Progression in Participants With Pelizaeus-Merzbacher Disease — Recruiting now
• Orbit Study: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Participants With Pelizaeus Merzbacher Disease (PMD) — Recruiting now
• An Extension Study of Donidalorsen (IONIS-PKK-LRx) in Participants With Hereditary Angioedema — Completed
• A Study to Assess the Long-Term Safety and Efficacy of Donidalorsen in the Prophylactic Treatment of Hereditary Angioedema (HAE) — Running, not enrolling
• OASIS-HAE: A Study to Evaluate the Safety and Efficacy of Donidalorsen (ISIS 721744 or IONIS-PKK-LRx) in Participants With Hereditary Angioedema (HAE) — Completed
• The APPROACH Study: A Study of Volanesorsen (Formerly IONIS-APOCIIIRx) in Patients With Familial Chylomicronemia Syndrome — Completed