Hopital Femme Mere-Enfant

Bron 69677

1 studies enrolling now · 4 studies all time

What they study most

Cystic Fibrosis, Muscular Dystrophy, Duchenne, OTC Deficiency, Spinal Muscular Atrophy

Studies at this site

• Clinical Study of DTX301 AAV-Mediated Gene Transfer for Ornithine Transcarbamylase (OTC) Deficiency — Running, not enrolling
• Evaluation of Long-Term Safety and Efficacy of Vanzacaftor/Tezacaftor/Deutivacaftor in Cystic Fibrosis Participants 1 Year of Age and Older — Enrolling by invitation
• A Study to Compare Safety and Efficacy of High Doses of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) (MIS51ON) — Running, not enrolling
• A Study of Risdiplam (RO7034067) in Adult and Pediatric Participants With Spinal Muscular Atrophy — Completed