Clinical Trial Site
Le Kremlin-Bicêtre 94270
3 studies enrolling now · 8 studies all time
What they study most
ATTR Amyloidosis, Amyloid Neuropathies, Amyloid Neuropathies, Familial, Amyloidosis, Amyloidosis, Hereditary, Amyloidosis, Hereditary, Transthyretin-Related, Atypical Hemolytic-Uremic Syndrome, Familial Amyloid Polyneuropathies, Hereditary Transthyretin-Mediated Amyloidosis With Polyneuropathy, TTR-mediated Amyloidosis, Transthyretin Amyloidosis, Transthyretin-Mediated Amyloidosis
Studies at this site
- TRITON-PN: A Study to Evaluate the Efficacy and Safety of Nucresiran in Patients With Hereditary Transthyretin Amyloidosis With Polyneuropathy — Recruiting now
- ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis) — Recruiting now
- Atypical Hemolytic-Uremic Syndrome (aHUS) Registry — Recruiting now
- HELIOS-A: A Study of Vutrisiran (ALN-TTRSC02) in Patients With Hereditary Transthyretin Amyloidosis (hATTR Amyloidosis) — Completed
- APOLLO: The Study of an Investigational Drug, Patisiran (ALN-TTR02), for the Treatment of Transthyretin (TTR)-Mediated Amyloidosis — Completed
- The Study of ALN-TTR02 (Patisiran) for the Treatment of Transthyretin (TTR)-Mediated Amyloidosis in Patients Who Have Already Been Treated With ALN-TTR02 (Patisiran) — Completed
- Safety and Tolerability of Patisiran (ALN-TTR02) in Transthyretin (TTR) Amyloidosis — Completed
- The Study of an Investigational Drug, Patisiran (ALN-TTR02), for the Treatment of Transthyretin (TTR)-Mediated Amyloidosis in Participants Who Have Already Been Treated With ALN-TTR02 (Patisiran) — Completed