The Study of an Investigational Drug, Patisiran (ALN-TTR02), for the Treatment of Transthyretin (TTR)-Mediated Amyloidosis in Participants Who Have Already Been Treated With ALN-TTR02 (Patisiran)
Completed · Phase 3 · Has a placebo group
Conditions studied: Amyloidosis
In brief
The purpose of this study is to evaluate the safety and efficacy of long-term dosing with ALN-TTR02 (patisiran) in participants with transthyretin (TTR) mediated amyloidosis (ATTR).
Key facts
- Study ID
- NCT02510261
- Run by
- Alnylam Pharmaceuticals
- People needed
- 211
- Starts
- 2015-07-16
- Expected to finish
- 2022-11-23
- Last updated by the study team
- 2023-12-06
Who can join
Age: 18 and older, up to 85. Sex: any. Healthy volunteers: not accepted.
You may qualify if…
- Have completed a patisiran study (i.e., completed the last efficacy visit in the parent study) and, in the opinion of the investigator, tolerated study drug
- Be willing and able to comply with the protocol-required visit schedule and visit requirements and provide written informed consent
You may not qualify if…
- Any new or uncontrolled condition that could make the participant unsuitable for participation
Where it is running
- Clinical Trial Site — Aurora, Colorado, United States
- Clinical Trial Site — Jacksonville, Florida, United States
- Clinical Trial Site — Chicago, Illinois, United States
- Clinical Trial Site — Baltimore, Maryland, United States
- Clinical Trial Site — Boston, Massachusetts, United States
- Clinical Trial Site — Detroit, Michigan, United States
- Clinical Trial Site — Rochester, Minnesota, United States
- Clinical Trial Site — Joplin, Missouri, United States
- Clinical Trial Site — St Louis, Missouri, United States
- Clinical Trial Site — Cooperstown, New York, United States
- Clinical Trial Site — New York, New York, United States
- Clinical Trial Site — New York, New York, United States
- Clinical Trial Site — Columbus, Ohio, United States
- Clinical Trial Site — Buenos Aires, Argentina
- Clinical Trial Site — Westmead, Australia
- Clinical Trial Site — Rio de Janeiro, Brazil
- Clinical Trial Site — São Paulo, Brazil
- Clinical Trial Site — Sofia, Bulgaria
- Clinical Trial Site — Vancouver, British Columbia, Canada
- Clinical Trial Site — Nicosia, Cyprus
- Clinical Trial Site — Fort de France, Martinique, France
- Clinical Trial Site — Saint-Pierre, Reunion Island, France
- Clinical Trial Site — Créteil, France
- Clinical Trial Site — Le Kremlin-Bicêtre, France
- Clinical Trial Site — La Mesa, California, United States
Full record on ClinicalTrials.gov
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