Rady Childrens Hospital

San Diego, California 92132

36 studies enrolling now · 157 studies all time

What they study most

ATP-Binding Cassette Subfamily C Member 6 Deficiency, Acinetobacter Baumannii-calcoaceticus Complex Infection (ABC), Acne Vulgaris, Acute Kidney Failure, Acute Kidney Injury, Acute Leukemia of Ambiguous Lineage, Acute Liver Failure, Acute Liver Injury, Acute Lymphoblastic Leukemia, Acute Myelogenous Leukemia, Acute Myeloid Leukemia, Acute Otitis Media

Studies at this site

• Adding Dasatinib Or Venetoclax To Improve Responses In Children With Newly Diagnosed T-Cell Acute Lymphoblastic Leukemia (ALL) Or Lymphoma (T-LLY) Or Mixed Phenotype Acute Leukemia (MPAL) — Recruiting now
• A Phase 3 Trial to Compare IV BCV Versus IV CDV for Treatment of Adenovirus Infection After Allo-HCT — Recruiting now
• A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy — Recruiting now
• A Study of DB-OTO, an Adeno-Associated Virus (AAV) Based Gene Therapy, in Children/Infants, Adolescents and Adults With Hearing Loss Due to Otoferlin Mutations — Recruiting now
• Study of Revumenib, Azacitidine, and Venetoclax in Pediatric and Young Adult Patients With Refractory or Relapsed Acute Myeloid Leukemia — Recruiting now
• REVEAL: A Phase 3 Study of ION582 in Angelman Syndrome — Recruiting now
• BEACON - Phase III Clinical Study of Rugonersen in Angelman Syndrome. — Recruiting now
• Clinical and Basic Investigations Into Congenital Disorders of Glycosylation — Recruiting now
• Identification of Necessary Information for Treatment Induction in Newly Diagnosed Acute Lymphoblastic Leukemia/Lymphoma — Recruiting now
• Prevention of Bleeding in Patients With Moderate and Severe Hemophilia A Playing Sports: A Comparison Between Factor VIII and Emicizumab Prophylaxis — Recruiting now
• Silmitasertib (CX-4945) in Combination With Chemotherapy for Relapsed Refractory Solid Tumors — Recruiting now
• Naxitamab Added to Induction for Newly Diagnosed High-Risk Neuroblastoma — Recruiting now
• Study of 2 Medicines (Aztreonam and Avibactam) Compared to Best Available Therapy for Serious Gram-negative Infections — Recruiting now
• DFMO as Maintenance Therapy for Molecular High/Very High Risk and Relapsed Medulloblastoma — Recruiting now
• Pediatric Precision Laboratory Advanced Neuroblastoma Therapy — Recruiting now
• Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy — Recruiting now
• Individualized Treatment Plan in Children and Young Adults With Relapsed Medulloblastoma and Ependymoma — Recruiting now
• Safety Study of Unlicensed IND Cord Blood Units Manufactured by the National Cord Blood Program for Unrelated Transplantation — Recruiting now
• ATTUNE: A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Intrathecally-Administered ION440 in Participants With Methyl CpG Binding Protein 2 (MECP2) Duplication Syndrome (MDS) — Recruiting now
• Targeted Reversal of Inflammation in Pediatric Sepsis-induced MODS — Recruiting now
• A Study to Assess Sulbactam-durlobactam in Pediatric Patients With Acinetobacter Baumannii-calcoaceticus Complex Infection — Recruiting now
• Beat Childhood Cancer Specimen Banking and Data Registry — Recruiting now
• HALOS: A Safety, Tolerability, Pharmacokinetics and Pharmacodynamics Study of Multiple Ascending Doses of ION582 in Participants With Angelman Syndrome — Recruiting now
• Fontan Udenafil Exercise Longitudinal Assessment Trial - 2 — Recruiting now
• Dance Mental Health App — Recruiting now
• Quality of Pediatric Resuscitation in a Multicenter Collaborative — Recruiting now
• OMEGA: Outcome Measures in Eosinophilic Gastrointestinal Disorders Across the Ages — Recruiting now
• National Collaborative to Improve Care of Children With Complex Congenital Heart Disease — Recruiting now
• Cardiotoxicity Assessment Through Comprehensive Heart Imaging to Predict Heart Failure — Recruiting now
• Prospective Multicenter Evaluation of a New Predictive Model for the Progression of Adolescent Idiopathic Scoliosis — Recruiting now
• The Tether™ - Vertebral Body Tethering System Post Approval Study — Recruiting now
• The ENERGY Study: Evaluation of Safety and Tolerability of INZ-701 in Infants With ENPP1 Deficiency or ABCC6 Deficiency — Running, not enrolling
• A Trial of Setmelanotide in Acquired Hypothalamic Obesity — Running, not enrolling
• TReatment for ImmUne Mediated PathopHysiology — Running, not enrolling
• A Study of Orforglipron (LY3502970) Compared With Dulaglutide in Pediatric Participants With Type 2 Diabetes — Starting soon
• Eflornithine (DFMO) and Etoposide for Relapsed/Refractory Neuroblastoma — Running, not enrolling
• Long-term Safety and Efficacy of Odevixibat in Patients With Alagille Syndrome — Running, not enrolling
• Efficacy and Safety of Odevixibat in Children With Biliary Atresia Who Have Undergone a Kasai HPE (BOLD) — Completed
• The Hunger Elimination or Reduction Objective (HERO ) Open -Label Extension (OLE) Trial — Stopped early
• Phase II Study Incorporating Pegylated Interferon In the Treatment For Children With High-Risk Melanoma — Running, not enrolling
• Study of Efficacy and Safety of Tisagenlecleucel in HR B-ALL EOC MRD Positive Patients — Running, not enrolling
• Study of Tenofovir Alafenamide (TAF) in Children and Teen Participants With Chronic Hepatitis B Virus Infection — Running, not enrolling
• Phase 2 Study of LUM-201 in Children With Growth Hormone Deficiency (OraGrowtH210 Trial) — Completed
• Immunotherapy Before and After Surgery for Treatment of Recurrent or Progressive High Grade Glioma in Children and Young Adults — Running, not enrolling
• Neuroblastoma Maintenance Therapy Trial — Running, not enrolling
• A Study in the United Sates That Looks at the Safety and Effectiveness of Pradaxa Pellets in Children Aged 3 Months to Less Than 12 Years Who Need Treatment of a Blood Clot or Who Have Had a Blood Clot and Are at Risk of Developing Another Blood Clot — Stopped early
• Risk-Adapted Therapy for Young Children With Embryonal Brain Tumors, Choroid Plexus Carcinoma, High Grade Glioma or Ependymoma — Running, not enrolling
• Phase 2 Study of LUM-201 in Children Who Have Previously Completed the LUM-201-01 Trial (OraGrowtH213) — Completed
• Expanded Access Program for Tiratricol in Patients With Monocarboxylate Transporter 8 Deficiency — Available (expanded access)
• Roll-over Study to Collect and Assess Long-term Safety of Everolimus in Patients With TSC and Refractory Seizures Who Have Completed the EXIST-3 Study [CRAD001M2304] and Who Are Benefitting From Continued Treatment — Running, not enrolling