Ospedale Pediatrico Bambino Gesu'

Rome 50

5 studies enrolling now · 16 studies all time

What they study most

Accelerated Phase Chronic Myelogenous Leukemia, Acute Kidney Injury, Adenovirus Infections, Alagille Syndrome, Becker Muscular Dystrophy, Blastic Phase Chronic Myelogenous Leukemia, C3 Glomerulonephritis, C3 Glomerulopathy, C3G, Cholestatic Liver Disease (Except ALGS, PFIC, PBC and PSC), Chronic Phase Chronic Myelogenous Leukemia, Complement 3 Glomerulonephritis

Studies at this site

• Long-Term Follow-up Protocol for Participants Treated With Gene-Modified T Cells — Recruiting now
• A Phase 3 Trial to Compare IV BCV Versus IV CDV for Treatment of Adenovirus Infection After Allo-HCT — Recruiting now
• A Study to Learn More About the Long-Term Safety of BIIB141 (Omaveloxolone) in Participants With Friedreich's Ataxia Who Are Prescribed it by Their Own Doctors — Recruiting now
• Long-term Safety and Efficacy of Odevixibat in Patients With Alagille Syndrome — Running, not enrolling
• Long-term Follow-up Study for Participants of Kite-Sponsored Interventional Studies Treated With Gene-Modified Cells — Enrolling by invitation
• Evaluation of Maralixibat in Pruritus Associated With General Cholestatic Liver Disease (EXPAND) — Running, not enrolling
• Observational Study of Pediatric Acute Kidney Injury, Risk Factors and Outcomes — Completed
• Phase III Study Assessing the Efficacy and Safety of Pegcetacoplan in Patients With C3 Glomerulopathy or Immune-Complex Membranoproliferative Glomerulonephritis — Completed
• Interventional Study of Vosoritide for the Treatment of Children With Hypochondroplasia — Running, not enrolling
• Bosutinib in Pediatric Patients With Newly Diagnosed Chronic Phase or Resistant/Intolerant Ph + Chronic Myeloid Leukemia — Running, not enrolling
• Long-Term Extension Study of Vosoritide to Treat Children With Hypochondroplasia — Enrolling by invitation
• Study Evaluating the Long-term Safety and Efficacy of VX-445 Combination Therapy — Completed
• A Study for Long-term Follow-up of Hemophagocytic Lymphohistiocytosis (HLH) Participants Who Received Treatment With Emapalumab (NI-0501), an Anti-interferon Gamma Monoclonal Antibody — Completed
• A Phase 3 Study of VX-445 Combination Therapy in Cystic Fibrosis (CF) Subjects Heterozygous for F508del and a Gating or Residual Function Mutation (F/G and F/RF Genotypes) — Completed
• Extension Study of Ataluren in Participants With Nonsense Mutation Cystic Fibrosis — Stopped early
• Phase 2B Study of PTC124 (Ataluren) in Duchenne/Becker Muscular Dystrophy (DMD/BMD) — Completed