Great Ormond Street Hospital (GOSH)

London WC1N3JH

0 studies enrolling now · 7 studies all time

What they study most

Duchenne Muscular Dystrophy, Hemophilia A, Muscular Dystrophy, Duchenne, Thrombotic Microangiopathies

Studies at this site

• Study of SRP-4045 (Casimersen) and SRP-4053 (Golodirsen) in Participants With Duchenne Muscular Dystrophy (DMD) — Completed
• Nomacopan (rVA576) in Transplant Associated Thrombotic Microangiopathy — Stopped early
• An Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular Dystrophy — Stopped early
• Phase III Study of Edasalonexent in Boys With Duchenne Muscular Dystrophy — Completed
• Non-interventional Post-authorisation Study to Document the Immunogenicity, Safety, and Efficacy of NUWIQ — Completed
• Efficacy and Safety Study of WVE-210201 (Suvodirsen) With Open-label Extension in Ambulatory Patients With Duchenne Muscular Dystrophy — Stopped early
• An Open-Label Extension Study of Edasalonexent in Boys With Duchenne Muscular Dystrophy — Stopped early