An Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular Dystrophy

Stopped early · Phase 3

Conditions studied: Duchenne Muscular Dystrophy

In brief

The main objective of this study is to evaluate the safety and tolerability of long-term treatment with casimersen or golodirsen in patients with Duchenne muscular dystrophy (DMD).

Key facts

Study ID

NCT03532542

Run by

Sarepta Therapeutics, Inc.

People needed

171

Starts

2018-08-02

Expected to finish

2023-07-26

Last updated by the study team

2024-09-19

Who can join

Age: 7 and older, up to 23. Sex: male. Healthy volunteers: not accepted.

You may qualify if…

• Completed a clinical trial evaluating casimersen or golodirsen, per protocol.
• Is between 7 and 23 years of age, inclusive, at enrollment.
• Other inclusion/exclusion criteria apply.

Where it is running

• Neuromuscular Research Center — Phoenix, Arizona, United States
• Children's Hospital Los Angeles — Los Angeles, California, United States
• University of California Los Angeles — Los Angeles, California, United States
• Stanford Neuroscience Health Center — Palo Alto, California, United States
• Rady Children's Hospital- San Diego — San Diego, California, United States
• UF Health: University of Florida Clinical Research Center — Gainesville, Florida, United States
• NW Florida Clinical Research Group, LLC — Gulf Breeze, Florida, United States
• Rare Disease Research, LLC — Atlanta, Georgia, United States
• Ann and Robert H Lurie Childrens Hospital of Chicago — Chicago, Illinois, United States
• University of Iowa Childrens Hospital — Iowa City, Iowa, United States
• University of Kansas Medical Center — Kansas City, Kansas, United States
• Kennedy Krieger Institute — Baltimore, Maryland, United States
• Boston Children's Hospital — Boston, Massachusetts, United States
• St. Louis Children's Hospital — St Louis, Missouri, United States
• Las Vegas Clinic — Las Vegas, Nevada, United States
• University of Rochester Medical Center - Department of Neurology — Rochester, New York, United States
• Cincinnati Children's Hospital Medical Center — Cincinnati, Ohio, United States
• Abigail Wexner Research Institute at Nationwide Children's Hospital — Columbus, Ohio, United States
• Shriners Hospital for Children — Portland, Oregon, United States
• Children's Hospital of Pittsburgh of UPMC — Pittsburgh, Pennsylvania, United States
• Children's Medical Center Dallas — Dallas, Texas, United States
• Texas Children's Hospital — Houston, Texas, United States
• University of Utah - PPDS — Salt Lake City, Utah, United States
• Children's Hospital of The King's Daughters — Norfolk, Virginia, United States
• Children's Hospital of Wisconsin, Corporate Center Suite 540 — Milwaukee, Wisconsin, United States

Full record on ClinicalTrials.gov

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