Clinical Trial Site

Zagreb 10000

1 studies enrolling now · 2 studies all time

What they study most

Acid Cholesteryl Ester Hydrolase Deficiency, Type 2, Acid Lipase Deficiency, Cholesterol Ester Storage Disease, LAL-Deficiency, LIPA Deficiency, Lysosomal Acid Lipase Deficiency, Transthyretin Amyloidosis (ATTR) With Cardiomyopathy, Wolman Disease

Studies at this site

• Lysosomal Acid Lipase (LAL) Deficiency Registry — Recruiting now
• HELIOS-B: A Study to Evaluate Vutrisiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy — Running, not enrolling