Clinical Trial Site

Riyadh 14611

2 studies enrolling now · 3 studies all time

What they study most

Acid Cholesteryl Ester Hydrolase Deficiency, Type 2, Acid Lipase Deficiency, Cholesterol Ester Storage Disease, Generalized Myasthenia Gravis, LAL-Deficiency, LIPA Deficiency, Lysosomal Acid Lipase Deficiency, Transthyretin Amyloidosis (ATTR) With Cardiomyopathy, Wolman Disease

Studies at this site

• Lysosomal Acid Lipase (LAL) Deficiency Registry — Recruiting now
• Registry of Participants With Generalized Myasthenia Gravis Treated With Alexion C5 Inhibition Therapies (C5ITs) — Recruiting now
• HELIOS-B: A Study to Evaluate Vutrisiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy — Running, not enrolling