Clinical Trial Site
Nantes 44093
3 studies enrolling now · 6 studies all time
What they study most
ANCA-Associated Vasculitis, Acid Cholesteryl Ester Hydrolase Deficiency, Type 2, Acid Lipase Deficiency, Amyloidosis, Hereditary, Atypical Hemolytic-Uremic Syndrome, Cholesterol Ester Storage Disease, Hereditary Transthyretin-mediated (hATTR) Amyloidosis, LAL-Deficiency, LIPA Deficiency, Lysosomal Acid Lipase Deficiency, Polyneuropathy, Surgery
Studies at this site
- Patisiran-Lipid Nanoparticle (LNP) Pregnancy Surveillance Program — Recruiting now
- Lysosomal Acid Lipase (LAL) Deficiency Registry — Recruiting now
- Atypical Hemolytic-Uremic Syndrome (aHUS) Registry — Recruiting now
- HELIOS-A: A Study of Vutrisiran (ALN-TTRSC02) in Patients With Hereditary Transthyretin Amyloidosis (hATTR Amyloidosis) — Completed
- A Phase 3 Clinical Trial of CCX168 (Avacopan) in Patients With ANCA-Associated Vasculitis — Completed
- Trial of Andexanet in Patients Receiving an Oral FXa Inhibitor Who Require Urgent Surgery — Stopped early