Clinical Trial Site
Manhasset, New York 11030
1 studies enrolling now · 4 studies all time
What they study most
ALA Dehydratase Deficient Porphyria (ADP), Acute Hepatic Porphyria, Acute Intermittent Porphyria (AIP), Dermatomyositis, Hepatic Porphyrias, Hereditary Coproporphyria (HCP), Porphyria Acute, Transthyretin Amyloidosis (ATTR) With Cardiomyopathy, Transthyretin Amyloidosis With Cardiomyopathy, Variegate Porphyria (VP)
Studies at this site
- TRITON-CM: A Study to Evaluate Nucresiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy — Recruiting now
- A Study to Investigate the Efficacy and Safety of Brepocitinib in Adults With Dermatomyositis — Running, not enrolling
- HELIOS-B: A Study to Evaluate Vutrisiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy — Running, not enrolling
- INSIGHT-AHP: A Study to Characterize the Prevalence of Acute Hepatic Porphyria (AHP) in Patients With Clinical Presentation and History Consistent With AHP — Stopped early