Clinical Trial Site
Chapel Hill, North Carolina 27599
3 studies enrolling now · 8 studies all time
What they study most
ANCA-Associated Vasculitis, AQP4+ NMOSD, Amyloidosis, Hereditary, Generalized Myasthenia Gravis, Hereditary Hemorrhagic Telangiectasia, Hereditary Transthyretin-Mediated Amyloidosis With Polyneuropathy, Hereditary Transthyretin-mediated (ATTRv) Amyloidosis, NMOSD, Neuromyelitis Optica, Neuromyelitis Optica Spectrum Disorder, Polyneuropathy, Transthyretin Amyloidosis
Studies at this site
- TRITON-PN: A Study to Evaluate the Efficacy and Safety of Nucresiran in Patients With Hereditary Transthyretin Amyloidosis With Polyneuropathy — Recruiting now
- Registry of Patients With AQP4+ NMOSD Treated With Alexion C5 Inhibitor Therapies — Recruiting now
- Registry of Participants With Generalized Myasthenia Gravis Treated With Alexion C5 Inhibition Therapies (C5ITs) — Recruiting now
- A Study to Evaluate ALN-6400 in Healthy Volunteers and Patients With Hereditary Hemorrhagic Telangiectasia (HHT) — Running, not enrolling
- HELIOS-A: A Study of Vutrisiran (ALN-TTRSC02) in Patients With Hereditary Transthyretin Amyloidosis (hATTR Amyloidosis) — Completed
- A Phase 3 Clinical Trial of CCX168 (Avacopan) in Patients With ANCA-Associated Vasculitis — Completed
- A Study of the Safety and Activity of Eculizumab in Pediatric Participants With Relapsing Neuromyelitis Optica Spectrum Disorder — Stopped early
- A Multicenter Observational Study to Evaluate the Effectiveness of Patisiran in Patients With Polyneuropathy of ATTRv Amyloidosis With a V122I or T60A Mutation — Completed