Childrens Hospital of Philadelphia (CHOP)
Philadelphia, Pennsylvania 19178
7 studies enrolling now · 28 studies all time
What they study most
22q11 Deletion Syndrome, Acute Migraine, Alport Syndrome, Atypical Hemolytic Uremic Syndrome, BK Virus Infection, Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy, Crohn's Disease, Cystic Fibrosis, Desmoplastic Small Round Cell Tumor, Diabetes Mellitus, Diabetes Mellitus, Type 1, Diabetes Mellitus, Type 2
Studies at this site
- A Master Protocol (AMAZ): A Study of Mirikizumab (LY3074828) in Pediatric Participants With Ulcerative Colitis or Crohn's Disease (SHINE-ON) — Recruiting now
- A Study of Baricitinib (LY3009104) to Preserve Beta Cell Function in Children and Adults Newly Diagnosed With Type 1 Diabetes (BARICADE-PRESERVE) — Recruiting now
- A Study of Baricitinib (LY3009104) for the Delay of Stage 3 Type 1 Diabetes in At-Risk Children and Adults — Recruiting now
- A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B — Recruiting now
- Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT — Recruiting now
- Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia — Recruiting now
- Epilepsy Learning Healthcare System (ELHS) — Recruiting now
- CAMPFIRE: A Study of Ramucirumab (LY3009806) in Children and Young Adults With Desmoplastic Small Round Cell Tumor — Completed
- Natural History Study Protocol in PMM2-CDG (CDG-Ia) — Completed
- The ASCEND Study: Evaluating TMB-001 in the Treatment of RXLI or ARCI Ichthyosis — Completed
- A Study of Abemaciclib (LY2835219) in Combination With Other Anti-Cancer Treatments in Children and Young Adult Participants With Solid Tumors, Including Neuroblastoma — Completed
- A Safety Study for Previously Treated Vatiquinone (PTC743) Participants With Inherited Mitochondrial Disease — Completed
- A Study to Evaluate Tirzepatide (LY3298176) in Pediatric and Adolescent Participants With Type 2 Diabetes Mellitus Inadequately Controlled With Metformin or Basal Insulin or Both — Completed
- A Patient Registry Study for Patients Treated With Voretigene Neparvovec in US — Completed
- Fimepinostat in Treating Brain Tumors in Children and Young Adults — Running, not enrolling
- A Phase 2/3 Trial of the Efficacy and Safety of Bardoxolone Methyl in Patients With Alport Syndrome - CARDINAL — Completed
- ATHN 7: Hemophilia Natural History Study — Completed
- NB-001 in Children and Adolescents With 22q11 Deletion Syndrome — Completed
- Crizotinib (Xalkori) Expanded Access Protocol For The Treatment Of Adult Or Pediatric Patients — NO_LONGER_AVAILABLE
- Study to Evaluate Viralym-M (ALVR105) for the Treatment of Virus-Associated Hemorrhagic Cystitis (HC) — Stopped early
- Eculizumab to Treat Thrombotic Microangiopathy/Atypical Hemolytic Uremic Syndrome -Associated Multiple Organ Dysfunction Syndrome in Hematopoietic Stem Cell Transplant Recipients — Completed
- Exercise in Genetic Cardiovascular Conditions — Completed
- Assessing Physician and Hemophilia A Patient Reasons and Expectations for Switching Treatment to Kovaltry & Jivi: A Nested Study Within an Existing Registry — Stopped early
- ATHN 2: Factor Switching Study — Completed
- Anti-CD3 mAb Treatment of Recent Onset Type 1 Diabetes — Completed
- Safety and Efficacy of Nerivio™ for the Acute Treatment of Migraine in Adolescents — Stopped early
- A Study to Evaluate Pharmacokinetics of Tafluprost Ophthalmic Solution (0.0015%) in Pediatric Patients With Glaucoma or Ocular Hypertension — Completed
- Study of LYM-X-SORB™ to Improve Fatty Acid and Choline Status in Children With CF and PI — Completed