A Long-term Follow-up Study in Patients Who Received BEAM-101

Recruiting now

Conditions studied: Hemoglobinopathy, Sickle Cell Disease

In brief

This is a Long-term Follow-up (LTFU) study in patients who received BEAM-101 in the parent study (Study BTX-AUT-001). Eligible patients who received BEAM-101 will be asked to participate in this LTFU study prior to completing Study BTX-AUT-001. Patients who enter into this study will be followed for 13 years (a total of 15 years after receiving BEAM-101).

Key facts

Study ID

NCT07373639

Run by

Beam Therapeutics Inc.

People needed

50

Starts

2025-12-15

Expected to finish

2043-02-12

Last updated by the study team

2026-01-28

Who can join

Age: 14 and older, up to 37. Sex: any. Healthy volunteers: not accepted.

You may qualify if…

• Have received BEAM-101 in Study BTX-AUT-001 and are in the process of completing that study's end-of-study (EOS) visit.
• Provide signed, written informed consent according to local institutional review board (IRB)/independent ethics committee (IEC) and institutional requirements.

You may not qualify if…

• There are no exclusion criteria for this study.

Where it is running

• Boston Children's Hospital — Boston, Massachusetts, United States (enrolling)
• Phoenix Children's Hospital — Phoenix, Arizona, United States
• Mayo Clinic Florida — Jacksonville, Florida, United States
• Children's Healthcare of Atlanta - Aflac Cancer and Blood Disorders Center- Egleston — Atlanta, Georgia, United States
• Henry Ford Cancer Center — Detroit, Michigan, United States
• University of Minnesota — Minneapolis, Minnesota, United States
• Washington University School of Medicine in St. Louis — St Louis, Missouri, United States
• Hackensack University Medical Center — Hackensack, New Jersey, United States
• Columbia University Irving Medical Center — New York, New York, United States
• University Hospitals Clevland Medical Center — Cleveland, Ohio, United States
• The Clevland Clinic Foundation — Cleveland, Ohio, United States
• Children's Hospital of Philadelphia — Philadelphia, Pennsylvania, United States
• Medical University of South Carolina — Charleston, South Carolina, United States
• St. Jude Children's Research Hospital — Memphis, Tennessee, United States
• The Children's Hospital at TriStar Centennial — Nashville, Tennessee, United States
• University of Alabama at Birmingham — Birmingham, Alabama, United States
• Medical College of Wisconsin — Milwaukee, Wisconsin, United States

Full record on ClinicalTrials.gov

Trial information comes from ClinicalTrials.gov and is refreshed daily. TrialsForMe does not provide medical care and does not run the studies it lists.