Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients
Recruiting now · Phase 2 · Has a placebo group
Conditions studied: Duchenne Muscular Dystrophy, Duchenne, DMD, Neuromuscular Diseases, Muscular Dystrophies
In brief
Phase 2a trial of SAT-3247 in ambulatory DMD patients aged ≥ 7 and \< 10 years. The trial will study two doses of SAT-3247 in a randomized, double-blind, placebo-controlled weekday regimen for 12 weeks to determine the optimal dose, safety, tolerability, and preliminary efficacy.
Key facts
- Study ID
- NCT07287189
- Run by
- Satellos Bioscience, Inc.
- People needed
- 51
- Starts
- 2025-12-08
- Expected to finish
- 2027-06-30
- Last updated by the study team
- 2026-07-31
Who can join
Age: 7 and older, up to 9. Sex: male. Healthy volunteers: not accepted.
Where it is running
- Great Ormond Street — London, UK, United Kingdom (enrolling)
- Colorado Children's — Aurora, Colorado, United States (enrolling)
- Lurie Children's — Chicago, Illinois, United States (enrolling)
- UMass Memorial Medical Center — Worcester, Massachusetts, United States (enrolling)
- Washington University — St Louis, Missouri, United States (enrolling)
- Nationwide Children's Hospital — Columbus, Ohio, United States (enrolling)
- Seattle Children's — Seattle, Washington, United States (enrolling)
- Children's Hospital at Westmead — Westmead, New South Wales, Australia (enrolling)
- Royal Children's Hospital Melbourne — Melbourne, Victoria, Australia (enrolling)
- Hôpital De La Citadelle (CHR) — Liège, Liège, Belgium (enrolling)
- UZ Gent — Ghent, Oost-Vlaanderen, Belgium (enrolling)
- Children's Hospital Eastern Ontario — Ottawa, Ontario, Canada (enrolling)
- Klinika Neurologii Rozwojowej Uniwersyteckie — Gdansk, Pomeranian Voivodeship, Poland (enrolling)
- Instytut Centrum Zdrowia Matki Polki — Lodz, Łódź Voivodeship, Poland (enrolling)
- Hospital Universitario y Politécnico La Fe — Valencia, Valencia, Spain (enrolling)
- Hospital Infantil i Hospital de la Dona — Barcelona, Spain (enrolling)
- University of California Los Angeles — Los Angeles, California, United States (enrolling)
- Mother and Child Health Care Institute — Belgrade, Serbia, Serbia (enrolling)
- Clinic of Neurology and Psychiatry for Children and Youth — Belgrade, Serbia, Serbia
- University Children's Clinic Tirsova — Belgrade, Serbia, Serbia
- Hospital Universitario Donostia — Donostia / San Sebastian, Basque Country, Spain
Full record on ClinicalTrials.gov
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