Low Dose Treosulfan Based Conditioning Regimen and PTCy in HSCT for Nijmegen Breakage Syndrome

Recruiting now · Phase 2

Conditions studied: Nijmegen Breakage Syndrome

In brief

The aim of the current study is to evaluate the safety and efficacy of low dose treosulfan based conditioning regimen in HSCT with post-transplant cyclophosphamide in Nijmegen breakage syndrome

Key facts

Study ID

NCT06198842

Run by

Federal Research Institute of Pediatric Hematology, Oncology and Immunology

People needed

10

Starts

2023-11-22

Expected to finish

2029-01-31

Last updated by the study team

2024-01-10

Who can join

Age: 0 and older, up to 21. Sex: any. Healthy volunteers: not accepted.

You may qualify if…

• Patients aged ≥ 3 months and < 21 years
• Patients diagnosed with NBS eligible for an allogeneic HSCT
• Signed written informed consent signed by a parent or legal guardian

Where it is running

• HSCT department — Moscow, Russia (enrolling)

Full record on ClinicalTrials.gov

Trial information comes from ClinicalTrials.gov and is refreshed daily. TrialsForMe does not provide medical care and does not run the studies it lists.