AMX0035 in Adult Patients With Wolfram Syndrome

Running, not enrolling · Phase 2

Conditions studied: Wolfram Syndrome

In brief

This study is an open label Phase II study to evaluate the safety and efficacy of AMX0035 in adults with Wolfram syndrome.

Key facts

Study ID

NCT05676034

Run by

Amylyx Pharmaceuticals Inc.

People needed

12

Starts

2023-03-03

Expected to finish

2028-05-31

Last updated by the study team

2026-04-14

Who can join

Age: 17 and older. Sex: any. Healthy volunteers: not accepted.

Where it is running

• Washington University — St Louis, Missouri, United States

Full record on ClinicalTrials.gov

Trial information comes from ClinicalTrials.gov and is refreshed daily. TrialsForMe does not provide medical care and does not run the studies it lists.