Limb-Girdle Video Assessment

Stopped early

Conditions studied: Limb-Girdle Muscular Dystrophy ; Subtypes 2A, 2B, and 2I

In brief

The purpose of this study is to develop a new remote-based video assessment outcome measure for Limb-Girdle Muscular Dystrophy (LGMD) trials. The overall objectives for this study are: 1. Identify domains and tasks meaningful to participants with a Limb-Girdle Muscular Dystrophy (LGMD) for development of the LGVA, including considerations for subtype heterogeneity and functional subgroup branching; 2. Determine the feasibility and reliability of the LGVA with test-retest of the LGVA Video Capture Manual; 3. Assess and refine the LGVA Video Capture Manual to ensure standardization and incorporate feedback from participants; 4. Collect source material videos using the LGVA Video Capture Manual to support the development of scorecards for the LGVA.

Key facts

Study ID
NCT05528757
Run by
The Emmes Company, LLC
People needed
45
Starts
2022-06-20
Expected to finish
2022-11-02
Last updated by the study team
2023-12-18

Who can join

Age: 14 and older. Sex: any. Healthy volunteers: not accepted.

Where it is running

Full record on ClinicalTrials.gov

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