Long-term Follow-up Study of Patients Who Received hLB-001 Gene Therapy

Running, not enrolling

Conditions studied: Methylmalonic Acidemia

In brief

This is a non-interventional long-term follow-up study of patients who have participated in LogicBio studies for the treatment of MMA and received hLB-001

Key facts

Study ID

NCT05506254

Run by

Alexion Pharmaceuticals, Inc.

People needed

4

Starts

2022-07-15

Expected to finish

2037-01-01

Last updated by the study team

2026-02-05

Who can join

Age: 18 and older. Sex: any. Healthy volunteers: not accepted.

You may qualify if…

• Participant has previously participated in a LogicBio clinical trial and received hLB-001.

You may not qualify if…

• None

Where it is running

• Clinical Trial Site — Atlanta, Georgia, United States
• Clinical Trial Site — Pittsburgh, Pennsylvania, United States
• Clinical Trial Site — Nashville, Tennessee, United States
• Clinical Trial Site — Seattle, Washington, United States

Full record on ClinicalTrials.gov

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