Extension Study of Oral PHA-022121 for Acute Treatment of Angioedema Attacks in Patients With Hereditary Angioedema
Enrolling by invitation · Phase 2/Phase 3 · Has a placebo group
Conditions studied: Hereditary Angioedema, Hereditary Angioedema Type I, Hereditary Angioedema Type II, Hereditary Angioedema Types I and II, Hereditary Angioedema Attack, Hereditary Angioedema With C1 Esterase Inhibitor Deficiency, Hereditary Angioedema - Type 1, Hereditary Angioedema - Type 2, Hereditary Angioedema - Type 3, C1 Esterase Inhibitor [C1-INH] Deficiency, C1 Esterase Inhibitor Deficiency, C1 Esterase Inhibitor, Deficiency of, C1 Inhibitor Deficiency, Hereditary Angioedema Type III, Hereditary Angioedema (HAE), Hereditary Angioedema Type I and II, HAE With Normal C1 Esterase Inhibitor
In brief
This study evaluates the safety and efficacy of long-term on-demand treatment with orally administered deucrictibant for acute hereditary angioedema (HAE) attacks, including laryngeal attacks. The study will enroll participants from Study PHA022121-C201 (NCT04618211), Study PHA022121-C306 (NCT06343779) and deucrictibant treatment naïve HAE-nC1INH adult participants who elect to participate in this extension study and meet the eligibility requirements.
Key facts
- Study ID
- NCT05396105
- Run by
- Pharvaris Netherlands B.V.
- People needed
- 150
- Starts
- 2022-12-28
- Expected to finish
- 2027-06-01
- Last updated by the study team
- 2026-07-21
Who can join
Age: 12 and older. Sex: any. Healthy volunteers: not accepted.
Where it is running
- Study site — Little Rock, Arkansas, United States
- Study site — San Diego, California, United States
- Study site — Santa Monica, California, United States
- Study site — Walnut Creek, California, United States
- Study site — Colorado Springs, Colorado, United States
- Study site — Chevy Chase, Maryland, United States
- Study site — Boston, Massachusetts, United States
- Study site — Detroit, Michigan, United States
- Study site — St Louis, Missouri, United States
- Study site — Hershey, Pennsylvania, United States
- Study site — Dallas, Texas, United States
- Study site — Buenos Aires, Argentina
- Study site — Salta, Argentina
- Study site — Campbelltown, New South Wales, Australia
- Study site — Graz, Austria
- Study site — Vienna, Austria
- Study site — Salvador, Estado de Bahia, Brazil
- Study site — Ribeirão Preto, Brazil
- Study site — Santo André, Brazil
- Study site — São Paulo, Brazil
- Study site — Sofia, Bulgaria
- Study site — Sofia, Bulgaria
- Study site — Edmonton, Alberta, Canada
- Study site — Montreal, Quebec, Canada
- Study site — Birmingham, Alabama, United States
Full record on ClinicalTrials.gov
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