International Registry of Patients With Alpha Thalassemia

Recruiting now

Conditions studied: Alpha-Thalassemia, Alpha Thalassemia Major, Alpha Thalassemia Minor

In brief

This is an international prospective registry of patients with Alpha thalassemia to understand the natural history of the disease and the outcomes of fetal therapies, with the overall goal of improving the prenatal management of patients with Alpha thalassemia.

Key facts

Study ID

NCT04872179

Run by

University of California, San Francisco

People needed

500

Starts

2017-01-01

Expected to finish

2037-01-01

Last updated by the study team

2025-04-04

Who can join

Age: any. Sex: any. Healthy volunteers: not accepted.

You may qualify if…

• diagnosis of alpha thalassemia (prenatal or postnatal) with genotype consistent with ATM or BHFS phenotype
• referred to the University of California, San Francisco Fetal Treatment Center for fetal diagnosis, management and/or evaluation for the ongoing in utero stem cell transplantation clinical trial

You may not qualify if…

• none

Where it is running

• University of California San Francisco — San Francisco, California, United States (enrolling)

Full record on ClinicalTrials.gov

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