Open-Label Extension: Tolerability and Effects of ALK-001 on Stargardt Disease (TEASE)

Running, not enrolling · Phase 2

Conditions studied: Stargardt Disease, Stargardt Macular Degeneration, Stargardt Macular Dystrophy, Autosomal Recessive Stargardt Disease 1 (ABCA4-related)

In brief

The purpose of this open-label, multicenter study is to determine the long-term safety, pharmacokinetics and effects of ALK-001 (C20-D3-retinyl acetate) on the progression of Stargardt disease. This study is an extension of NCT02402660 and enrolls participants who are at least 8 years old. Enrollment is by invitation only. Funding Source - FDA OOPD

Key facts

Study ID
NCT04239625
Run by
Alkeus Pharmaceuticals, Inc.
People needed
200
Starts
2019-12-20
Expected to finish
2026-12-01
Last updated by the study team
2025-04-27

Who can join

Age: 8 and older, up to 70. Sex: any. Healthy volunteers: not accepted.

Where it is running

Full record on ClinicalTrials.gov

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