Long Term Extension Study in Patients With Primary Hyperoxaluria
Running, not enrolling · Phase 3
Conditions studied: Primary Hyperoxaluria Type 1 (PH1), Primary Hyperoxaluria Type 2 (PH2), Kidney Diseases, Urologic Diseases, Genetic Disease, Primary Hyperoxaluria Type 3 (PH3)
In brief
The proposed study is designed to provide patients previously enrolled in Phase 1 and 2 studies of DCR-PHXC and their siblings (\<18 years old) long-term access to DCR-PHXC, and to evaluate the long-term safety and efficacy of DCR-PHXC in patients with PH.
Key facts
- Study ID
- NCT04042402
- Run by
- Dicerna Pharmaceuticals, Inc., a Novo Nordisk company
- People needed
- 75
- Starts
- 2019-07-09
- Expected to finish
- 2030-04-01
- Last updated by the study team
- 2025-05-30
Who can join
Age: any. Sex: any. Healthy volunteers: not accepted.
Where it is running
- Clinical Research Site — San Francisco, California, United States
- Clinical Trial Site — Boston, Massachusetts, United States
- Clinical Trial Site — Rochester, Minnesota, United States
- Clinical Trial Site — New York, New York, United States
- Clinical Research Site — Herston, Queensland, Australia
- Clinical Trial Site — Melbourne, Australia
- Clinical Research Site — Hamilton, Ontario, Canada
- Clinical Trial Site — Bron, France
- Clinical Trial Site — Paris, France
- Clinical Trial Site — Bonn, Germany
- Clinical Trial Site — Heidelberg, Germany
- Clinical Research Site — Roma, Italy
- Clinical Trial Site — Fukuoka, Japan
- Clinical Trial Site — Nagoya, Japan
- Clinical Trial Site — Tokyo, Japan
- Clinical Trial Site — Beirut, Lebanon
- Clinical Trial Site — Amsterdam, Netherlands
- Clinical Trial Site — Tromsø, Norway
- Clinical Research Site — Barcelona, Spain
- Clinical Trial Site — Barcelona, Spain
- Clinical Trial Site — Ankara, Turkey (Türkiye)
- Clinical Trial Site — Hampstead, London, United Kingdom
- Clinical Trial Site — Birmingham, United Kingdom
Full record on ClinicalTrials.gov
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