Effect of Nusinersen on Adults With Spinal Muscular Atrophy

Completed

Conditions studied: Adult Spinal Muscular Atrophy

In brief

Observational study of adult patients with spinal muscular atrophy types 2 and 3 receiving nusinersen

Key facts

Study ID

NCT03878030

Run by

Northwell Health

People needed

12

Starts

2019-04-01

Expected to finish

2021-07-13

Last updated by the study team

2023-03-20

Who can join

Age: 18 and older, up to 60. Sex: any. Healthy volunteers: not accepted.

You may qualify if…

• Genetically confirmed 5q SMA
• ability to access intrathecal space for nusinersen injection

You may not qualify if…

• Renal impairment
• thrombocytopenia
• inability to access intrathecal space by CT or flouro guided injection

Where it is running

• Northwell Health Neuroscience — Great Neck, New York, United States

Full record on ClinicalTrials.gov

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