Expanded Access to Mepsevii

Available (expanded access)

Conditions studied: MPS VII, Mucopolysaccharidosis VII, Sly Syndrome

In brief

Individual patient expanded access requests may be considered for patients who have no other treatment options

Key facts

Study ID

NCT03775174

Run by

Ultragenyx Pharmaceutical Inc

Last updated by the study team

2026-07-30

Who can join

Age: any. Sex: any. Healthy volunteers: not accepted.

Full record on ClinicalTrials.gov

Trial information comes from ClinicalTrials.gov and is refreshed daily. TrialsForMe does not provide medical care and does not run the studies it lists.