An Efficacy and Safety Study of Palovarotene for the Treatment of MO
Stopped early · Phase 2 · Has a placebo group
Conditions studied: Exostoses, Multiple Hereditary
In brief
This is a randomized, double-blind, placebo-controlled study comparing the safety and efficacy of 2 dosage regimens of palovarotene versus placebo in preventing disease progression in pediatric subjects with multiple osteochondromas (MO).
Key facts
- Study ID
- NCT03442985
- Run by
- Clementia Pharmaceuticals Inc.
- People needed
- 193
- Starts
- 2018-03-22
- Expected to finish
- 2020-10-30
- Last updated by the study team
- 2022-08-01
Who can join
Age: 2 and older, up to 14. Sex: any. Healthy volunteers: not accepted.
Where it is running
- Children's Orthopaedic Center — Los Angeles, California, United States
- Shriners Hospital for Children - Sacramento — Sacramento, California, United States
- University of California-San Francisco — San Francisco, California, United States
- Children's National Medical Center — Washington D.C., District of Columbia, United States
- The Paley Institute — West Palm Beach, Florida, United States
- Shriners Hospital for Children - Chicago — Chicago, Illinois, United States
- Johns Hopkins University — Baltimore, Maryland, United States
- Boston Children's Hospital — Boston, Massachusetts, United States
- Mayo Clinic - PPDS — Rochester, Minnesota, United States
- Shriners Hospitals for Children - Portland — Portland, Oregon, United States
- The Children's Hospital of Philadelphia (CHOP) — Philadelphia, Pennsylvania, United States
- Shriners Hospital for Children - Philadelphia — Philadelphia, Pennsylvania, United States
- Memorial Hermann Hospital — Houston, Texas, United States
- Westmead Children's Hospital — Westmead, New South Wales, Australia
- UZ Antwerpen — Edegem, Antwerp, Belgium
- Hospital for Sick Children — Toronto, Ontario, Canada
- Centre Hospitalier Universitaire Sainte-Justine — Montreal, Quebec, Canada
- Shriners Hospital for Children - Canada — Montreal, Quebec, Canada
- Hôpital universitaire Necker - Enfants Malades — Paris, France
- Hôpital des Enfants, CHU de Toulouse — Toulouse, France
- Istituti Ortopedici Rizzoli — Bologna, Emilia-Romagna, Italy
- Nagoya University Hospital — Nagoya, Aiti, Japan
- Osaka University Hospital — Suita, Osaka, Japan
- OLVG locatie Oost — Amsterdam, North Holland, Netherlands
- Hospital Pediátrico de Coimbra — Coimbra, Portugal
Full record on ClinicalTrials.gov
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