A Study of ARRY-371797 (PF-07265803) in Patients With Symptomatic Dilated Cardiomyopathy Due to a Lamin A/C Gene Mutation
Stopped early · Phase 3 · Has a placebo group
Conditions studied: Dilated Cardiomyopathy, Lamin A/C Gene Mutation
In brief
This is a randomized, double-blind, placebo-controlled study in patients with dilated cardiomyopathy (DCM) due to a mutation of the gene encoding the lamin A/C protein (LMNA). The study will further evaluate a dose level of study drug (ARRY-371797) that has shown preliminary efficacy and safety in this patient population. After the primary analysis has been performed, eligible patients may receive open-label treatment with ARRY-371797.
Key facts
- Study ID
- NCT03439514
- Run by
- Pfizer
- People needed
- 77
- Starts
- 2018-04-17
- Expected to finish
- 2022-10-13
- Last updated by the study team
- 2024-01-09
Who can join
Age: 18 and older. Sex: any. Healthy volunteers: not accepted.
Where it is running
- University of Alabama at Birmingham the Kirklin Clinic — Birmingham, Alabama, United States
- IDS Pharmacy at UAB Hospital — Birmingham, Alabama, United States
- Cardiovascular Clinical Trials Unit — Birmingham, Alabama, United States
- CB Flock Research Corporation — Mobile, Alabama, United States
- Chandler Regional Medical Center — Chandler, Arizona, United States
- Valley Heart Rhythm Specialists, PLLC — Chandler, Arizona, United States
- Cardiovascular and Stem Cell Consultants — Gilbert, Arizona, United States
- Cardiovascular Research Clinic — Gilbert, Arizona, United States
- Dignity Health, Mercy Gilbert Medical Center — Gilbert, Arizona, United States
- Mercy Gilbert Medical Center — Gilbert, Arizona, United States
- Children's Clinic — Tucson, Arizona, United States
- Banner - Banner University Medical Center South — Tucson, Arizona, United States
- Banner - University Medical Center Tucson — Tucson, Arizona, United States
- Banner University Medicine North — Tucson, Arizona, United States
- Banner University Medical Center Tuscon — Tucson, Arizona, United States
- University of Arizona Sarver Heart Center — Tucson, Arizona, United States
- Ahmanson Cardiomyopathy Center Cardiovascular Genetics — Los Angeles, California, United States
- Stanford Hospital and Clinics — Stanford, California, United States
- University of Colorado Academic Offices Building — Aurora, Colorado, United States
- University of Colorado Clinical and Translational Research Center — Aurora, Colorado, United States
- University of Colorado Hospital — Aurora, Colorado, United States
- Medstar Washington Hospital Center — Washington D.C., District of Columbia, United States
- Innovative Research of West Florida — Clearwater, Florida, United States
- University of South Florida — Tampa, Florida, United States
- University of Alabama at Birmingham Hospital — Birmingham, Alabama, United States
Full record on ClinicalTrials.gov
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