Long-Term Follow-Up Gene Therapy Study for Achromatopsia CNGB3 and CNGA3

Stopped early

Conditions studied: Achromatopsia

In brief

This is a longer-term follow-up study of patients with achromatopsia associated with defects in CNGA3 who participated in a clinical trial in which they received AAV-CNGA3 retinal gene therapy, or of patients with achromatopsia associated with defects in CNGB3 who participated in a clinical trial in which they received AAV-CNGB3 retinal gene therapy.

Key facts

Study ID
NCT03278873
Run by
MeiraGTx UK II Ltd
People needed
34
Starts
2017-06-29
Expected to finish
2024-04-04
Last updated by the study team
2025-06-11

Who can join

Age: 3 and older, up to 100. Sex: any. Healthy volunteers: not accepted.

Where it is running

Full record on ClinicalTrials.gov

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