Natural History Study of Patients With Leber Congenital Amaurosis Associated With Mutations in RPE65

Completed

Conditions studied: Leber Congenital Amaurosis

In brief

MGT005 is a natural history study to collect longitudinal prospective data from patients with Leber Congenital Amaurosis associated with defects in RPE65.

Key facts

Study ID

NCT02714816

Run by

MeiraGTx UK II Ltd

People needed

37

Starts

2016-04-01

Expected to finish

2023-07-22

Last updated by the study team

2023-08-14

Who can join

Age: 3 and older. Sex: any. Healthy volunteers: not accepted.

You may qualify if…

• Patients with RPE65 associated retinal dystrophy
• Minimum subject age of 3 years
• Able to give consent/parent or guardian able to give consent

You may not qualify if…

• Patients unable or unwilling to undertake consent or clinical testing
• Have received a gene therapy treatment in both eyes

Where it is running

• Kellogg Eye Center — Ann Arbor, Michigan, United States
• Moorfields Eye Hospital — London, United Kingdom

Full record on ClinicalTrials.gov

Trial information comes from ClinicalTrials.gov and is refreshed daily. TrialsForMe does not provide medical care and does not run the studies it lists.