Study to Evaluate the Safety, Efficacy, and Pharmacokinetics of Recombinant Coagulation Factor VIII Fc Fusion Protein (rFVIIIFc) in Previously Treated Pediatric Subjects With Hemophilia A
Completed · Phase 3
Conditions studied: Hemophilia A
In brief
The primary objective of the study is to evaluate the safety of Recombinant Coagulation Factor VIII Fc Fusion Protein (rFVIIIFc) in previously treated pediatric subjects with hemophilia A. Secondary objectives of this study in this study population are as follows: to evaluate the efficacy of rFVIIIFc for prevention and treatment of bleeding episodes; to evaluate and assess the pharmacokinetics (PK) of rFVIIIFc; and to evaluate rFVIIIFc consumption for prevention and treatment of bleeding episodes.
Key facts
- Study ID
- NCT01458106
- Run by
- Bioverativ Therapeutics Inc.
- People needed
- 71
- Starts
- 2012-11-01
- Expected to finish
- 2013-12-01
- Last updated by the study team
- 2020-12-19
Who can join
Age: any, up to 11. Sex: male. Healthy volunteers: not accepted.
Where it is running
- Research Site — Los Angeles, California, United States
- Research Site — Sacramento, California, United States
- Research Site — San Diego, California, United States
- Research Site — Aurora, Colorado, United States
- Research Site — Chicago, Illinois, United States
- Research Site — Indianapolis, Indiana, United States
- Research Site — St Louis, Missouri, United States
- Research Site — Las Vegas, Nevada, United States
- Research Site — Cincinnati, Ohio, United States
- Research Site — Columbus, Ohio, United States
- Research Site — Portland, Oregon, United States
- Research Site — Pittsburgh, Pennsylvania, United States
- Research Site — Brisbane, Queensland, Australia
- Research Site — Melbourne, Victoria, Australia
- Research Site — Hong Kong, Hong Kong
- Research Site — Dublin, Ireland
- Research Site — Groningen, Netherlands
- Research Site — Lublin, Poland
- Research Site — Johannesburg, South Africa
- Research Site — Cambridge, Cambridgshire, United Kingdom
- Research Site — Basingstoke, Hampshire, United Kingdom
- Research Site — Glasgow, United Kingdom
- Research Site — London, United Kingdom
Full record on ClinicalTrials.gov
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