Vall d'Hebron Barcelona Hospital Campus
Barcelona, Barcelona 08035
1 studies enrolling now ยท 1 studies all time
What they study most
MPS IIIA, Mucopolysaccharidosis III, Sanfilippo A, Sanfilippo Syndrome
Studies at this site
- Phase I/II/III Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH โ Recruiting now