Vall d'Hebron Barcelona Campus
Barcelona 08035
1 studies enrolling now ยท 1 studies all time
What they study most
MPS IIIA, Mucopolysaccharidosis IIIA, Sanfilippo A, Sanfilippo Syndrome
Studies at this site
- Follow-up Study of AAV-Mediated Gene Transfer (UX111; Previously Known as ABO-102) for MPS Type IIIA โ Enrolling by invitation