UT Southwestern Children's Medical Center

Dallas, Texas 75930

1 studies enrolling now · 2 studies all time

What they study most

Mucopolysaccharidosis (MPS) IIIC, Rett Syndrome, Sanfilippo Syndrome Type C

Studies at this site

• Natural History to Assess Disease in Patients With MPS IIIC — Starting soon
• A Phase 1/2/3 Study of TSHA-102 Gene Therapy in Females With Rett Syndrome (REVEAL Pivotal Study) — Running, not enrolling