UPMC Hospital of Pittsburgh

Pittsburgh, Pennsylvania 15224

1 studies enrolling now · 1 studies all time

What they study most

Glycogen Storage Disease Type II Infantile Onset

Studies at this site

• A Study to Evaluate the Safety, Efficacy, PK, PD and Immunogenicity of Cipaglucosidase Alfa/Miglustat in IOPD Subjects Aged 0 to <18 — Recruiting now