UPMC Children's Hospital Pittburgh

Pittsburgh, Pennsylvania 15224

1 studies enrolling now · 2 studies all time

What they study most

MPS III B, Mucopolysaccharidosis Type IIIB

Studies at this site

• Safety, Tolerability and Efficacy of ICV AX 250 Treatment in MPS IIIB -OLE — Enrolling by invitation
• A Treatment Extension Study of Mucopolysaccharidosis Type IIIB — Status unconfirmed